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Voxzogo
Pharma
BioMarin halts dosing, enrollment in 3 midstage Voxzogo studies
BioMarin will discontinue dosing and enrollment of its phase 2 trials for Voxzogo—approved for a form of dwarfism—across three indications.
Fraiser Kansteiner
Mar 16, 2026 11:26am
FDA approves Ascendis' achondroplasia treatment Yuviwel
Mar 2, 2026 9:25am
BioMarin pulls gene therapy Roctavian off the market
Feb 24, 2026 12:30pm
BioMarin touts pipeline asset as potential Voxzogo replacement
Aug 5, 2025 11:30am
BioMarin unveils strategic redesign under CEO Alexander Hardy
Sep 4, 2024 5:32pm
With slow sales, BioMarin weighs Roctavian divestiture
Apr 29, 2024 11:51am