Translarna

Pharma

Europe's CHMP backs Novo's FDA-rejected hemophilia treatment

The European drug reviewers gave a thumbs-up to Novo's FDA-rejected hemophilia treatment, but they turned down PTC Therapeutics' Translarna yet again.

Zoey Becker Oct 18, 2024 11:27am

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PTC gets another chance to keep Translarna's EU authorization

May 20, 2024 8:58am

PTC, after rejections, will try again with Translarna at the FDA

Mar 19, 2024 10:10am

European Union flags waving in front of the EU Parliament building in Brussels

PTC's re-examination bid for Translarna falls short in Europe

Jan 25, 2024 5:12pm

Market withdrawal looms for PTC's DMD drug in Europe

Sep 15, 2023 10:42am

NICE signs off on rare disease therapies from Alnylam, PTC

Jan 19, 2023 1:21pm