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PTC Therapeutics
Pharma
PTC wins FDA approval for brain-delivered gene therapy Kebilidi
The gene therapy has already been approved to treat AADC deficiency in Europe and the U.K., among other countries, where it's branded as Upstaza.
Zoey Becker
Nov 14, 2024 11:31am
Europe's CHMP backs Novo's FDA-rejected hemophilia treatment
Oct 18, 2024 11:27am
PTC gets another chance to keep Translarna's EU authorization
May 20, 2024 8:58am
PTC, after rejections, will try again with Translarna at the FDA
Mar 19, 2024 10:10am
The top 10 drugs losing US exclusivity in 2024
Mar 11, 2024 3:00am
PTC's Emflaza to face generics this month post Aurobindo FDA nod
Feb 12, 2024 10:10am
