Metabolic disorders

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Pharma

Mirum's Ctexli scores FDA approval in rare metabolic disorder

The FDA on Friday gave the green light to Mirum’s Ctexli for the treatment of adults with the rare metabolic disorder cerebrotendinous xanthomatosis.
Fraiser Kansteiner Feb 21, 2025 3:30pm
Liver doctor holding liver

Intercept's Ocaliva fails its 2nd NASH trial

Sep 30, 2022 11:49am