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lysosomal storage disorders
Pharma
Zevra pegs Miplyffa as 'cornerstone' of Niemann-Pick treatment
Zevra's commercial chief is confident that the company's new drug Miplyffa can become the “cornerstone” for treatment of Niemann-Pick disease type C.
Fraiser Kansteiner
Oct 4, 2024 6:45am
Zevra snags FDA approval for new lysosomal storage disorder med
Sep 20, 2024 1:54pm
DOJ probing BioMartin testing programs for Vimizim, Naglazyme
Feb 28, 2024 7:48am