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hematopoietic stem cells
Pharma
FDA signs off on 1st gene therapy for rare genetic disease
Fondazione Telethon's Waskyra is an ex vivo gene therapy that can address the root genetic cause of Wiskott-Aldrich syndrome.
Zoey Becker
Dec 10, 2025 12:09pm
In expansion bid, Astellas' Xospata comes up short again
Mar 9, 2023 10:11am