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gene therapy
Pharma
PTC wins FDA approval for brain-delivered gene therapy Kebilidi
The gene therapy has already been approved to treat AADC deficiency in Europe and the U.K., among other countries, where it's branded as Upstaza.
Zoey Becker
Nov 14, 2024 11:31am
Sarepta's Elevidys blows sales expectations out of the water
Nov 7, 2024 3:43pm
Consumer groups urge FTC to block Novo Holdings' Catalent deal
Oct 18, 2024 10:20am
AstraZeneca-CSPC, Astellas and more—Fierce Pharma Asia
Oct 11, 2024 9:48am
Ferring cuts ribbon at new gene therapy manufacturing hub
Oct 3, 2024 12:07pm
Bluebird bio lays off 25% of workforce
Sep 24, 2024 10:19am
