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enzyme disorders

Resarch Center Chiesi Farmaceutici SpA Parma
Pharma

5 years after European nod, Chiesi wins FDA approval for Lamzede

Five years after gaining approval in Europe for Lamzede, Chiesi Farmaceutici has pushed it over the finish line in the United States.
Kevin Dunleavy Feb 17, 2023 10:09am
Sanofi

FDA signs off on Sanofi's rare disease drug Xenpozyme

Aug 31, 2022 3:18pm
Sanofi Cambridge

Europe endorses two Sanofi enzyme replacement therapies

Jun 28, 2022 11:21am
Green light

Sanofi's late-onset Pompe prospect has scooped its green light

Aug 6, 2021 2:39pm
BioMarin building

BioMarin scores long-sought FDA nod for PKU drug

May 25, 2018 11:51am

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