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BridgeBio
Pharma
FDA approves Ascendis' achondroplasia treatment Yuviwel
The FDA has approved Ascendis' Yuviwel, a once-weekly injection to treat children with achondroplasia, a rare genetic disorder that causes dwarfism.
Kevin Dunleavy
Mar 2, 2026 9:25am
BridgeBio CEO shrugs off recent Attruby pricing pressure fears
Feb 25, 2026 2:30pm
Alnylam hits profitability in Q4 despite Amvuttra revenue miss
Feb 12, 2026 11:05am
BridgeBio shares slide on Pfizer's ATTR patent withdrawal
Feb 6, 2026 10:50am
Is Pfizer's recent ATTR sales decline in the US a warning sign?
Dec 2, 2025 8:20am
BioMarin touts pipeline asset as potential Voxzogo replacement
Aug 5, 2025 11:30am