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BioMarin Pharmaceutical
Pharma
BioMarin halts dosing, enrollment in 3 midstage Voxzogo studies
BioMarin will discontinue dosing and enrollment of its phase 2 trials for Voxzogo—approved for a form of dwarfism—across three indications.
Fraiser Kansteiner
Mar 16, 2026 11:26am
FDA approves Ascendis' achondroplasia treatment Yuviwel
Mar 2, 2026 9:25am
Fierce Biotech
Midsize biotechs form coalition to fight against MFN policy
Feb 25, 2026 1:05pm
BioMarin pulls gene therapy Roctavian off the market
Feb 24, 2026 12:30pm
BioMarin makes its largest transaction, paying $4.8B for Amicus
Dec 19, 2025 11:28am
BioMarin looks to drop hemophilia gene therapy Roctavian
Oct 28, 2025 11:49am