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beta thalassemia

Vertex
Pharma

Long-term data shows durability of Vertex's gene therapy Casgevy

At the European Hematology Association conference, Vertex presented long-term data showing the durability and effectiveness of gene therapy Casgevy.
Kevin Dunleavy Jun 14, 2024 11:12am
Vertex bluebird

Vertex's Casgevy launch progresses as CF drugs post solid growth

May 7, 2024 11:23am
CRISPR Therapeutics

FDA approves Vertex, CRISPR's Casgevy for beta thalassemia

Jan 16, 2024 3:40pm
Thalassemia

Agios charts broad path for oral thalassemia med after trial win

Jan 3, 2024 10:49am
Vertex

In 'historic' nod, UK signs off on Vertex, CRISPR's gene therapy

Nov 16, 2023 11:45am
germ line gene editing DNA pass down family tree inherit

Vertex teases launch plans for first CRISPR gene editing therapy

Feb 8, 2023 2:55pm

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