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beta thalassemia
Pharma
Vanda, Agios score holiday season FDA approvals
The FDA delivered a pair of holiday season nods, signing off on Agios’ Aqvesme for thalassemia and Vanda's motion sickness pill Nereus.
Kevin Dunleavy
Jan 2, 2026 11:33am
Long-term data shows durability of Vertex's gene therapy Casgevy
Jun 14, 2024 11:12am
Vertex's Casgevy launch progresses as CF drugs post solid growth
May 7, 2024 11:23am
FDA approves Vertex, CRISPR's Casgevy for beta thalassemia
Jan 16, 2024 3:40pm
Agios charts broad path for oral thalassemia med after trial win
Jan 3, 2024 10:49am
In 'historic' nod, UK signs off on Vertex, CRISPR's gene therapy
Nov 16, 2023 11:45am