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achondroplasia
Pharma
BioMarin touts pipeline asset as potential Voxzogo replacement
Competition is coming for BioMarin’s Voxzogo, but it may be able to answer with a longer-acting version of the drug, which treats a form of dwarfism.
Kevin Dunleavy
Aug 5, 2025 11:30am
For $100M, BridgeBio partners with Kyowa Kirin on infigratinib
Feb 7, 2024 12:53pm
BioMarin on its way to turning a profit in 2022
Apr 28, 2022 9:50am