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achondroplasia
Pharma
BioMarin halts dosing, enrollment in 3 midstage Voxzogo studies
BioMarin will discontinue dosing and enrollment of its phase 2 trials for Voxzogo—approved for a form of dwarfism—across three indications.
Fraiser Kansteiner
Mar 16, 2026 11:26am
FDA approves Ascendis' achondroplasia treatment Yuviwel
Mar 2, 2026 9:25am
BioMarin touts pipeline asset as potential Voxzogo replacement
Aug 5, 2025 11:30am
For $100M, BridgeBio partners with Kyowa Kirin on infigratinib
Feb 7, 2024 12:53pm
BioMarin on its way to turning a profit in 2022
Apr 28, 2022 9:50am